CRSP Tshuag: Thawj CRISPR Gene-Editing Tshuaj tuaj yeem nyob ntawm no sai dua li koj xav

Tshuaj Ntsuab Los Kho Ntau Yam (Crsp) tau hais rau hnub Tuesday nws yuav pib nug Lub Chaw Tswj Xyuas Khoom Noj thiab Tshuaj kom pom zoo dab tsi yuav yog thawj qhov kev kho gene-kho kho kom raug kev lag luam uas siv CRISPR thev naus laus zis los ntawm qhov chaw nws tau txais nws lub tuam txhab npe. CRSP Tshuag tau dhia.




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Rau kev pom zoo FDA, Crispr thiab tus khub Vertex Cov Kev Tshuaj (VRTX) tau hais tias lawv yuav pib xa lawv daim ntawv thov kev kho mob ntshav rau lub Kaum Ib Hlis. Lawv npaj yuav ua tiav cov txheej txheem ntawd hauv thawj peb lub hlis twg. Lawv tab tom nrhiav kev pom zoo hauv cov kab mob mob hlwb thiab beta thalassemia.

Lub sijhawm ncua sij hawm raug thawb rov qab me ntsis, tab sis qhov ntawd tsis zoo li yuav ua rau muaj kev lag luam sib txawv, RBC Capital Markets tus kws tshuaj ntsuam Brian Abrahams tau hais hauv tsab ntawv ceeb toom rau cov neeg siv khoom. Tseem, nws tseem ceev faj txog qhov kawg ntawm kev noj tshuaj, tam sim no dubbed exa-cel.

"Peb tseem khaws cia ntawm (exa-cel's) kev muag khoom muaj peev xwm txheeb ze rau (Vertex's) cov nyiaj tau los, "nws hais. Nws pom $ 550 lab hauv kev muag khoom mus sij hawm ntev.

Tab sis nyob rau hauv premarket trading ntawm hnub no lub khw lag luam, cov xov xwm prodded CRSP Tshuag 3.1% siab dua, nyob ze 63. Vertex Tshuag kuj nce 1.2% ze 280.

CRSP Tshuag: Cov ntaub ntawv mus sij hawm ntev xav tau

Abrahams muaj cov haujlwm ua haujlwm ntawm Vertex Tshuag thiab tsis muab qhov ntsuas rau CRSP Tshuag. Nws sau tseg no CRISPR gene-editing kho yuav tsum kom tus neeg mob ua ntej kev kho mob nrog ib daim ntawv ntawm chemotherapy. Nws tab tom tos txog cov tshuaj kho cov noob caj noob ces uas tsis xav tau cov kauj ruam no.

Crispr thiab Vertex tab tom siv gene-editing los kho tus neeg mob lub peev xwm los tsim cov ntshav qab zib. Hauv kev tshaj tawm cov ntaub ntawv tsis ntev los no, cov tuam txhab tau muaj cov ntaub ntawv kev nyab xeeb ntev rau 23 tus neeg mob thiab cov ntaub ntawv ob xyoos rau plaub tus neeg mob, nws hais. Qhov ntawd yog tawm ntawm 75 tus neeg mob tag nrho.

FDA yuav xav tau cov ntaub ntawv mus sij hawm ntev dua, Abrahams tau hais.

"Peb cia siab tias thaum kawg ntawm thawj peb lub hlis twg, lawv yuav tsum muaj kwv yees li 48 tus neeg mob ntawm ib xyoos thiab 23 tus neeg mob ntawm ob xyoos rov qab," nws hais.

CRSP Tshuag tseem zoo hauv qab nws 50-hnub txav nruab nrab raws li hnub Monday kaw, raws li MarketSmith.com.

Ua raws li Allison Gatlin ntawm Twitter ntawm @IBD_AGatlin.

KOJ UA LI CAS:

Kev ua lag luam poob rau lub lim tiam dhau los; Vim li cas IBD Tshuag Ntawm Hnub Neurocrine Biosciences Tsis Tau

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Ua Raws Li Qhov Khw Ua Ntej Thiab Tom Qab-Qhov Haujlwm Qhib Nrog IBD Cov Kws Tshaj Lij

Cov Khoom Cuam Tshuam Yuav Yooj Yim Thiab Saib Xyuas: IPOs Sab saum toj, Lub Kaus Loj Loj Thiab Cov Me Me, Cov Lus Qhia Loj Hlob

Tau qhov twg los: https://www.investors.com/news/technology/crsp-stock-the-first-crispr-gene-editing-drug-could-be-here-sooner-than-you-think/?src=A00220&yptr = yahoo